Canavan disease, a rare and fatal neurological disorder caused by a mutation in the ASPA gene, leads to a deficiency in the enzyme aspartoacylase.
Find HiRO at SCDM 2026 at Booth #526 HiRO is excited to announce our attendance…
Find HiRO at SCDM 2026 at Booth #526 HiRO is excited to announce our attendance…